DMD care considerations – improving outcomes for patients with DMD
The 2010 International Care Considerations for DMD Footnote 1 Footnote 2
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In 2010, the US CDC selected an international coalition of 84 experienced clinicians from relevant therapy areas to develop DMD care recommendations
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The resulting DMD Care Considerations Working Group presented their findings in two parts:
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Part 1: Diagnosis, and neuromuscular, rehabilitation, endocrine and gastrointestinal and nutritional management Footnote 1
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Part 2: Implementation of multidisciplinary care Footnote 1
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2010 – 2018
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Prolonged survival Footnotes Footnotes Footnotes Footnotes 3–6
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Greater emphasis on QoL Footnotes Footnotes Footnotes Footnotes 3–6
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Emerging genetic and molecular therapies Footnote 7
The 2018 updates Footnotes Footnotes Footnotes 8–10
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2014: Multidisciplinary steering committee established to update the 2010 DMD Care Considerations, to:
improve patient care in an era of prolonged survival
provide guidance on advances in assessments and interventions
consider the implications of emerging genetic and molecular therapies for DMD
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The committee identified three new topics to be included in the update:
Primary care and emergency management
Endocrine management
of care across lifespan