The following materials are intended for healthcare professionals. These materials have been developed and funded by PTC Therapeutics.
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PTC have developed these focused, two-page summaries to provide you with a digestible overview of the 2018 International Duchenne Care Considerations. Click on the summaries to view.
Access the full International Duchenne Care Considerations here.
Recent studies have also demonstrated the benefits of early glucocorticoid treatment, before significant physical decline.1-3
Preserved muscle strength and motor function4,5
Delayed loss of ambulation1,4
Preserved pulmonary function1,4,5
Avoidance of scoliosis surgery1,4,5
*compared to untreated patients
The 2018 International Care Guidelines recommends following an initial consultation with the family, a discussion regarding side effects and a nutritional consultation should occur before any glucocorticoid treatment is initiated.1 Well documented side effects of long-term corticosteroid use can include; weight gain and obesity, acne and warts, cushingoid features, growth retardation and delayed puberty, cataracts, immune/adrenal suppression, glucose intolerance, hypertension, adverse behavioural changes, gastro-oesophageal reflux, peptic ulcer, gastritis, osteoporosis and myoglobinuria.6
Click here for the International Duchenne Care Considerations summaries.
For your patient, this can mean leading a fulfilling, independent life into adulthood.
Studies have shown that early diagnosis and care can help slow Duchenne muscular dystrophy progression and minimise the risks and complications of the disease.1,2 Click here to find out how you can help drive a successful diagnostic journey.
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